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Company > Amicus Therapeutics Inc: Business Model, SWOT Analysis, and Competitors 2023

Amicus Therapeutics Inc: Business Model, SWOT Analysis, and Competitors 2023

Published: Apr 12, 2023

Inside This Article


    Amicus Therapeutics Inc is a prominent biopharmaceutical company focused on developing advanced therapies for rare and devastating diseases. This blog article provides a comprehensive analysis of their business model, SWOT analysis, and key competitors for the year 2023. By delving into their innovative approach, strategic partnerships, and commitment to patient-centric research, we aim to gain insights into their potential for growth and market dominance. Additionally, a detailed examination of their strengths, weaknesses, opportunities, and threats will shed light on their competitive landscape and potential challenges in the coming years.

    What You Will Learn:

    • Who owns Amicus Therapeutics Inc and the significance of ownership in a company's success.
    • The mission statement of Amicus Therapeutics Inc and its importance in guiding the company's strategic decisions.
    • How Amicus Therapeutics Inc generates revenue and sustains its business operations.
    • An explanation of the Business Model Canvas of Amicus Therapeutics Inc and how it helps understand the company's key activities, resources, and value proposition.
    • Insight into the competitors of Amicus Therapeutics Inc and their impact on the company's market position.
    • A SWOT analysis of Amicus Therapeutics Inc, including an evaluation of its strengths, weaknesses, opportunities, and threats.

    Who owns Amicus Therapeutics Inc?

    Major Shareholders

    Amicus Therapeutics Inc., a leading global biotechnology company focused on advanced therapies for rare and orphan diseases, has a diverse ownership structure. The company's ownership is distributed among various institutions, mutual funds, and individual investors.

    One of the largest shareholders of Amicus Therapeutics is Capital Research and Management Company, an American financial investment management firm. They currently hold a significant stake in the company, demonstrating their confidence in Amicus' potential for growth and success.

    Another major shareholder of Amicus Therapeutics is BlackRock, a renowned global investment management corporation. With their expertise and extensive network, BlackRock's investment in Amicus signifies the company's recognition of the biotech firm's innovative approach and promising products.

    Institutional Investors

    Apart from these major shareholders, several other institutional investors have a stake in Amicus Therapeutics. These include Vanguard Group, a leading provider of mutual funds and ETFs, and State Street Corporation, a financial services and bank holding company.

    Other notable institutional investors in Amicus Therapeutics include Wellington Management Company, a global investment management firm, and Fidelity Management and Research Company, a prominent asset management institution. These institutions' investment in Amicus reflects the company's potential for long-term growth and value creation.

    Individual Shareholders

    In addition to institutional investors, individual shareholders also play a significant role in Amicus Therapeutics' ownership structure. These individual investors, often comprising scientists, healthcare professionals, and biotech enthusiasts, demonstrate their belief in the company's mission and dedication to advancing treatments for rare diseases.

    By being a part of Amicus Therapeutics' ownership, these individual shareholders not only contribute financially but also provide valuable insights and perspectives that can help shape the company's strategies and direction.


    Amicus Therapeutics Inc. has a diverse ownership structure, with major institutional investors and individual shareholders holding significant stakes in the company. This broad ownership base demonstrates the widespread confidence and interest in Amicus' innovative approach to developing therapies for rare and orphan diseases. As the company continues to make advancements in its research and development, it is likely to attract even more investors who recognize the potential of its pipeline and the positive impact it can have on patients' lives.

    What is the mission statement of Amicus Therapeutics Inc?

    The Mission Statement of Amicus Therapeutics Inc: Pioneering Therapies for Rare Diseases

    Amicus Therapeutics Inc is a renowned biotechnology company that specializes in the development of innovative therapies for rare and devastating diseases. Their mission statement encapsulates their commitment to improving the lives of patients affected by these conditions.

    The mission statement of Amicus Therapeutics Inc can be summarized as follows:

    "We are dedicated to discovering, developing, and delivering advanced therapies that transform the lives of individuals living with rare diseases."

    Amicus Therapeutics Inc recognizes the unique challenges faced by patients with rare diseases, often characterized by limited treatment options and a lack of understanding. Their mission is focused on addressing these unmet medical needs by harnessing the power of science, innovation, and collaboration.

    Putting Patients First

    At the core of Amicus Therapeutics Inc's mission is the patient. They aim to prioritize the well-being and quality of life of those affected by rare diseases. By developing therapies that target the underlying cause of the diseases and alleviating their symptoms, Amicus Therapeutics Inc strives to make a significant impact on the lives of patients and their families.

    Pioneering Therapies

    Amicus Therapeutics Inc is driven by a pioneering spirit, constantly pushing the boundaries of scientific knowledge and innovation. They aim to lead the way in the development of transformative therapies that address the root cause of rare diseases, rather than merely treating their symptoms. By focusing on breakthrough science, Amicus Therapeutics Inc aims to make a lasting impact on the field of rare disease research and treatment.

    Collaboration and Partnerships

    Recognizing the complex nature of rare diseases, Amicus Therapeutics Inc understands the importance of collaboration. They actively seek partnerships with patients, healthcare professionals, advocacy groups, and other stakeholders to collectively advance the understanding, diagnosis, and treatment of rare diseases. By fostering a collaborative environment, Amicus Therapeutics Inc aims to accelerate the development and delivery of life-changing therapies.

    In conclusion, the mission statement of Amicus Therapeutics Inc reflects their dedication to improving the lives of individuals affected by rare diseases. Through pioneering therapies, patient-centric approaches, and collaborative partnerships, Amicus Therapeutics Inc aims to make a meaningful impact in the field of rare disease research and treatment.

    How does Amicus Therapeutics Inc make money?

    Revenue Streams

    Amicus Therapeutics Inc generates its revenue through various sources, primarily driven by its innovative therapies and strategic collaborations within the biopharmaceutical industry.

    1. Product Sales

    The company derives a significant portion of its revenue from the sales of its approved products. Amicus Therapeutics specializes in developing and commercializing advanced therapies to treat rare genetic diseases, such as Fabry disease and Pompe disease. These therapies, manufactured by the company, are marketed under different brand names and are distributed globally. As the demand for effective treatments for rare diseases continues to rise, the company's product sales contribute substantially to its overall revenue.

    2. Licensing and Royalties

    Amicus Therapeutics also generates revenue through licensing agreements and royalties. The company collaborates with other pharmaceutical companies, both domestically and internationally, to develop and commercialize therapies for various genetic disorders. Through these collaborations, Amicus Therapeutics licenses its proprietary technologies, expertise, and intellectual property to its partners. In return, the company receives upfront payments, milestone payments, and ongoing royalties based on the sales of licensed products. This revenue stream allows the company to leverage its innovative research and development capabilities while expanding its market reach.

    3. Research Grants and Funding

    Amicus Therapeutics actively pursues research grants and funding opportunities to support its ongoing research and development efforts. The company collaborates with academic institutions, government agencies, and non-profit organizations to secure grants and funding for specific research projects. These grants not only provide financial support but also validate the company's scientific approach and potential therapeutic breakthroughs. By securing research grants, Amicus Therapeutics can advance its pipeline of novel therapies without solely relying on internal funding.

    4. Strategic Partnerships and Collaborations

    The company forms strategic partnerships and collaborations with other biotechnology and pharmaceutical companies to accelerate its drug discovery and development programs. Through these partnerships, Amicus Therapeutics gains access to additional resources, expertise, and technologies that enhance its research capabilities. These collaborations often involve upfront payments, milestone payments, and potential future royalties, providing a significant source of revenue for the company. Additionally, these partnerships enable Amicus Therapeutics to tap into new markets, expand its product portfolio, and strengthen its competitive position in the industry.

    In summary, Amicus Therapeutics Inc generates revenue through a combination of product sales, licensing and royalties, research grants and funding, as well as strategic partnerships and collaborations. These diverse revenue streams enable the company to sustain its research and development efforts, expand its market presence, and continue providing innovative therapies for rare genetic diseases.

    Amicus Therapeutics Inc Business Model Canvas Explained


    The business model canvas is a strategic tool that enables organizations to visualize and analyze their business model. In this section, we will delve into the business model canvas of Amicus Therapeutics Inc, a biotechnology company focused on developing innovative therapies for rare diseases. By examining the various components of their business model, we will gain a better understanding of how Amicus Therapeutics operates and creates value in the pharmaceutical industry.

    Key Partnerships

    Amicus Therapeutics places great emphasis on establishing strategic partnerships to enhance its research and development capabilities. The company collaborates with academic institutions, patient advocacy groups, and other biotechnology companies to leverage their expertise and resources. These partnerships enable Amicus Therapeutics to access valuable scientific knowledge, share risks and costs, and accelerate the development of its therapies.

    Key Activities

    The key activities of Amicus Therapeutics revolve around the research, development, and commercialization of therapies for rare diseases. The company invests heavily in scientific research to understand the underlying causes of these diseases and identify potential treatment options. Additionally, Amicus Therapeutics conducts rigorous clinical trials to validate the safety and efficacy of its therapies. Once a therapy is approved, the company focuses on manufacturing, marketing, and distributing the treatment to patients in need.

    Value Proposition

    Amicus Therapeutics aims to provide innovative and effective therapies for individuals suffering from rare diseases. By leveraging its deep understanding of genetic disorders and advanced technologies, the company strives to develop treatments that address the underlying causes of these diseases, rather than just managing their symptoms. This unique approach sets Amicus Therapeutics apart from its competitors and offers hope to patients and their families who have limited treatment options.

    Customer Segments

    The primary customer segments for Amicus Therapeutics are patients suffering from rare diseases, healthcare providers, and payers such as insurance companies. The company focuses on developing therapies for specific genetic disorders, tailoring its products to meet the unique needs of each patient population. By targeting these niche markets, Amicus Therapeutics can better understand and serve the requirements of its customers while maximizing the impact of its therapies.


    Amicus Therapeutics utilizes various channels to reach its customers and deliver its therapies. The company works closely with healthcare providers to ensure that its treatments are accessible to patients. Additionally, Amicus Therapeutics engages in direct-to-patient marketing efforts, leveraging digital platforms and patient advocacy groups to raise awareness about its therapies. By employing a multi-channel approach, the company aims to reach a wider audience and ensure that its treatments are available to those who need them.

    Revenue Streams

    The revenue streams of Amicus Therapeutics primarily come from the sales of its therapies. The company generates revenues through both direct sales to patients and partnerships with pharmaceutical distributors. Additionally, Amicus Therapeutics may receive grants, research funding, and milestone payments from its collaborations and strategic partnerships. These diverse revenue streams provide the company with financial stability and the resources needed to continue its research and development efforts.

    Key Resources

    Amicus Therapeutics relies on various key resources to support its operations. Its team of talented scientists and researchers is a crucial resource for driving innovation and developing groundbreaking therapies. The company also invests in state-of-the-art laboratories, manufacturing facilities, and equipment to support its research and production processes. Furthermore, Amicus Therapeutics leverages its intellectual property portfolio, patents, and proprietary technologies to protect its innovations and secure a competitive advantage in the market.


    By examining the business model canvas of Amicus Therapeutics Inc, we gain insights into the key components that drive the company's success. Through strategic partnerships, innovative research, and a focus on patient needs, Amicus Therapeutics has positioned itself as a leader in the rare disease therapeutics market. With its customer-centric approach and commitment to scientific excellence, the company continues to make significant contributions to improving the lives of patients affected by genetic disorders.

    Which companies are the competitors of Amicus Therapeutics Inc?


    Amicus Therapeutics Inc. is a biotechnology company that focuses on developing therapies for rare and orphan diseases. With a strong focus on developing novel treatments for lysosomal storage disorders (LSDs), Amicus Therapeutics has made significant strides in the field. However, like any other company in the biotech industry, Amicus Therapeutics faces competition from other players in the market. In this section, we will explore some of the key competitors of Amicus Therapeutics Inc.

    Competitors of Amicus Therapeutics Inc.

    1. Sanofi Genzyme - Sanofi Genzyme, a subsidiary of Sanofi, is a major competitor of Amicus Therapeutics. The company has a strong presence in the rare disease space and has developed several therapies for lysosomal storage disorders, including Gaucher disease and Pompe disease. Sanofi Genzyme's extensive experience and established market presence make them a formidable competitor for Amicus Therapeutics.

    2. Shire (now part of Takeda Pharmaceutical Company Limited) - Shire, now a part of Takeda Pharmaceutical Company Limited, is another significant competitor in the field of rare diseases. Shire has a robust portfolio of therapies for various genetic disorders, such as Fabry disease and Hunter syndrome. With their extensive resources and expertise, Shire poses a considerable challenge to Amicus Therapeutics in the race to develop innovative treatments.

    3. Ultragenyx Pharmaceutical Inc. - Ultragenyx Pharmaceutical Inc. is a biopharmaceutical company that focuses on developing therapies for rare and ultra-rare diseases. They have a pipeline of investigational products targeting various lysosomal storage disorders, including mucopolysaccharidosis type 7 (MPS 7) and glycogen storage disease type II (Pompe disease). Ultragenyx's commitment to rare diseases makes them a direct competitor to Amicus Therapeutics.

    4. BioMarin Pharmaceutical Inc. - BioMarin Pharmaceutical Inc. is a global biotechnology company that develops and commercializes innovative therapies for rare genetic diseases. They have a strong presence in the lysosomal storage disorder space, with therapies approved for diseases such as mucopolysaccharidosis type I (MPS I) and mucopolysaccharidosis type II (MPS II). BioMarin's established market position and pipeline of potential treatments make them a significant competitor for Amicus Therapeutics.


    Amicus Therapeutics Inc. operates in a highly competitive industry, where several companies are vying to develop groundbreaking therapies for rare and orphan diseases. Sanofi Genzyme, Shire (now part of Takeda Pharmaceutical Company Limited), Ultragenyx Pharmaceutical Inc., and BioMarin Pharmaceutical Inc. are some of the key competitors of Amicus Therapeutics. While competition is fierce, the ultimate goal remains the same - to improve the lives of patients suffering from rare diseases and provide them with effective treatment options.

    Amicus Therapeutics Inc SWOT Analysis


    1. Innovative and advanced therapies: Amicus Therapeutics Inc is known for its focus on developing novel therapies for rare and devastating diseases. The company has a strong track record of innovation and has successfully developed several groundbreaking treatments.

    2. Strong pipeline: Amicus Therapeutics Inc has a robust pipeline of potential therapies in various stages of development. This diverse portfolio reduces the company's dependence on a single product and provides a strong foundation for future growth.

    3. Strategic partnerships: The company has established strategic partnerships with leading pharmaceutical companies and research institutions. These collaborations not only provide access to expertise and resources but also enhance the credibility and reach of Amicus Therapeutics Inc's therapies.

    4. Experienced management team: The company boasts a highly experienced management team with a deep understanding of the pharmaceutical industry. Their expertise and strategic decision-making have contributed significantly to the company's success.


    1. Limited market presence: Despite its innovative therapies, Amicus Therapeutics Inc has a relatively limited market presence compared to some of its competitors. This could be attributed to factors such as limited marketing efforts or challenges in gaining widespread adoption of their therapies.

    2. Dependency on regulatory approvals: The company's success heavily relies on obtaining regulatory approvals for its therapies. Delays or rejections in obtaining these approvals can significantly impact the company's financial performance and growth prospects.

    3. High research and development costs: Developing innovative therapies requires substantial investment in research and development. Amicus Therapeutics Inc's high R&D expenses can strain its financial resources, especially if there are delays in bringing therapies to market or obtaining necessary funding.


    1. Growing rare disease market: The market for rare disease therapies is expanding rapidly, driven by increased awareness, improved diagnostics, and favorable regulatory policies. Amicus Therapeutics Inc is well-positioned to capitalize on this opportunity with its focus on developing treatments for rare diseases.

    2. Potential for partnerships and collaborations: The pharmaceutical industry is witnessing a trend of increased collaboration and partnerships. Amicus Therapeutics Inc can explore strategic alliances with other companies to enhance its research capabilities, expand its product portfolio, and gain access to new markets.

    3. Emerging markets: The company has the potential to expand its market reach by targeting emerging markets. These markets offer significant growth opportunities due to the increasing prevalence of rare diseases and improving healthcare infrastructure.


    1. Intense competition: The pharmaceutical industry is highly competitive, with numerous players vying for market share. Amicus Therapeutics Inc faces competition from established pharmaceutical companies as well as emerging biotech firms. Intense competition can impact pricing, market access, and the success of the company's therapies.

    2. Regulatory challenges: The regulatory landscape for pharmaceutical companies is complex and subject to frequent changes. Compliance with evolving regulations can be a challenge for Amicus Therapeutics Inc, potentially affecting the timelines and costs associated with obtaining regulatory approvals.

    3. Intellectual property risks: Protecting intellectual property rights is crucial for pharmaceutical companies. Amicus Therapeutics Inc may face the risk of patent infringement or challenges to its patents, which can impact its ability to commercialize its therapies and maintain a competitive advantage.

    4. Economic and market uncertainties: Economic downturns, changes in healthcare policies, and market volatility can impact the demand for pharmaceutical products. Amicus Therapeutics Inc is not immune to these external factors, and fluctuations in the market can affect its financial performance and growth prospects.

    Key Takeaways

    • Amicus Therapeutics Inc is owned by various institutional investors, including Vanguard Group, BlackRock, and Fidelity Management & Research.
    • The mission statement of Amicus Therapeutics Inc is to develop innovative therapies for rare, devastating diseases, with a focus on genetic disorders and lysosomal storage disorders.
    • Amicus Therapeutics Inc generates revenue primarily through the sale of its approved products, such as Galafold, a treatment for Fabry disease.
    • The Business Model Canvas of Amicus Therapeutics Inc outlines key activities, partners, resources, and customer segments, highlighting the company's emphasis on research and development, strategic partnerships, and patient-centric approach.
    • Competitors of Amicus Therapeutics Inc include biopharmaceutical companies like Sanofi Genzyme, Shire, and Biomarin Pharmaceutical Inc.
    • A SWOT analysis of Amicus Therapeutics Inc reveals its strengths in innovative therapies, strong partnerships, and a dedicated research team. It also identifies weaknesses in financial dependence on a limited number of products, opportunities in expanding market reach, and threats from competition and regulatory challenges.


    In conclusion, Amicus Therapeutics Inc is a biopharmaceutical company that focuses on developing therapies for rare and devastating diseases. The company's mission is to improve the lives of patients through innovative science and compassionate care. Amicus Therapeutics Inc generates revenue through the sale of its approved therapies, as well as through partnerships and collaborations with other pharmaceutical companies.

    The company's business model canvas demonstrates a strong focus on research and development, with a commitment to delivering value to patients and investors. By leveraging its expertise in genetic diseases, Amicus Therapeutics Inc aims to create a sustainable and profitable business.

    In terms of competition, Amicus Therapeutics Inc faces competition from other biopharmaceutical companies working in the same therapeutic areas. Some of its main competitors include companies like Biomarin Pharmaceutical Inc, Alexion Pharmaceuticals Inc, and Vertex Pharmaceuticals Inc.

    A SWOT analysis of Amicus Therapeutics Inc reveals its strengths in innovative science and strong research capabilities, as well as opportunities in expanding its product portfolio and entering new markets. However, the company also faces challenges such as high research and development costs and the risk of regulatory hurdles.

    Overall, Amicus Therapeutics Inc is a promising player in the biopharmaceutical industry, with a clear mission and a solid business model. With its focus on rare diseases and dedication to improving patient lives, the company is well-positioned for future success.


    How to do a SWOT analysis on a company?

    To conduct a SWOT analysis on a company, follow these steps:

    1. Define the objective: Determine the purpose of the analysis. Are you evaluating the company's overall performance, a specific project, or a new market entry?

    2. Identify strengths: Identify the internal factors that give the company an advantage over its competitors. Consider its unique selling proposition, brand reputation, financial stability, talented workforce, patents, or strong customer relationships.

    3. Identify weaknesses: Examine the internal factors that put the company at a disadvantage. Look for areas where the company lacks resources, skills, or expertise compared to competitors. Consider high employee turnover, outdated technology, limited market share, or poor financial health.

    4. Identify opportunities: Analyze the external factors that could be advantageous to the company. Look for market trends, emerging technologies, regulatory changes, or new customer segments that the company can capitalize on.

    5. Identify threats: Analyze external factors that could negatively impact the company's performance. Consider competitors, changing consumer preferences, economic downturns, legal or political factors, or disruptive technologies that may pose a threat.

    6. SWOT matrix: Create a matrix or a table with four quadrants: strengths, weaknesses, opportunities, and threats. Populate each quadrant with the points identified in the previous steps.

    7. Prioritize: Evaluate the significance of each point in the SWOT matrix. Focus on the most critical factors that deserve attention and action.

    8. Develop strategies: Based on the SWOT analysis, develop strategies to leverage strengths, address weaknesses, pursue opportunities, and mitigate threats. Align these strategies with the company's overall goals and objectives.

    9. Implementation: Develop an action plan to execute the strategies. Assign responsibilities, set deadlines, and establish metrics to measure progress.

    10. Review and update: Regularly review and update the SWOT analysis to stay relevant and responsive to changes in the company's internal and external environment.

    Remember that a SWOT analysis is just a starting point and should be complemented with in-depth research and analysis to make informed decisions.

    What is the mission statement of amicus therapeutics?

    The mission statement of Amicus Therapeutics is: "To deliver transformative therapies to people living with rare diseases. We are committed to discovering, developing, and delivering high-quality medicines for those in need, with a focus on improving the lives of patients and their families."

    What is SWOT analysis according to Albert Humphrey?

    Albert Humphrey is a management consultant who is credited with developing the SWOT analysis framework. SWOT analysis stands for Strengths, Weaknesses, Opportunities, and Threats. According to Humphrey, SWOT analysis is a structured approach used to evaluate the internal and external factors that can influence the success of a project, business, or individual. It involves identifying and analyzing the strengths and weaknesses of an entity (internal factors) and the opportunities and threats in its external environment. This analysis helps in identifying strategic options, making informed decisions, and formulating effective strategies.

    What are the opportunities in a SWOT analysis?

    Opportunities in a SWOT analysis refer to external factors or circumstances that can be advantageous for a business or organization. These opportunities can be seen as favorable conditions or trends that can be leveraged to achieve strategic goals and growth. Here are some examples of opportunities in a SWOT analysis:

    1. Market growth: Identifying emerging markets or market segments with potential for expansion can present significant opportunities for businesses to increase their customer base and revenue.

    2. Technological advancements: New technologies can create opportunities to improve operational efficiency, develop innovative products or services, and gain a competitive edge in the market.

    3. Changing consumer preferences: Shifts in consumer behavior and preferences can present opportunities for companies to develop new products, adapt their marketing strategies, or enter new markets.

    4. Strategic alliances and partnerships: Collaborating with other companies or forming strategic alliances can provide opportunities for businesses to access new markets, share resources, expand distribution channels, and enhance their competitive position.

    5. Government policies and regulations: Changes in government policies, regulations, or incentives can create opportunities for businesses to capitalize on new markets, subsidies, or tax benefits.

    6. Economic conditions: Favorable economic conditions, such as low interest rates, increasing disposable income, or a growing economy, can create opportunities for businesses to expand, invest, or introduce new products or services.

    7. Industry trends and developments: Keeping up with industry trends and developments can help businesses identify new opportunities, stay ahead of competitors, and adapt their strategies accordingly.

    8. International markets: Expanding into international markets can provide opportunities for businesses to tap into new customer bases, access resources, and diversify revenue streams.

    9. Changing demographics: Understanding demographic shifts, such as an aging population or changing workforce dynamics, can help businesses identify opportunities to cater to specific needs and preferences.

    10. Competitive gaps: Identifying gaps in the market or weaknesses in competitors' offerings can create opportunities to develop differentiated products or services that meet customer demands.

    It is important for businesses to assess these opportunities and align them with their strengths to effectively capitalize on them and achieve their objectives.

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